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Allele-selective editing of mHTT utilizing AAV5-delivered Life Edit®️ CRISPR System (LETI-101) results in meaningful reduction of mHTT protein
// November 7, 2024 | 31st Annual Meeting of the Huntington Study Group Cincinnati, OH
Allele-selective editing of mHTT utilizing AAV5-delivered Life Edit®️ CRISPR System (LETI-101) results in meaningful reduction of mHTT protein